Gene Therapy for Hemophilia A: How Long Will It Last? Schutgens, Roger E. G. Schutgens, Roger E. G. Less HemaSphere. 6(6):e720, June 2022. Favorites PDF Get Content & Permissions Open
The EHA Research Roadmap: Hematopoietic Stem Cell Gene Therapy Naldini, Luigi; Cicalese, Maria Pia; Bernardo, Maria Ester; More Naldini, Luigi; Cicalese, Maria Pia; Bernardo, Maria Ester; Gentner, Bernhard; Gabaldo, Michela; Ferrari, Giuliana; Aiuti, Alessandro Less HemaSphere. 6(2):e671, February 2022. Favorites PDF Get Content & Permissions Open
Modeling Benefits, Costs, and Affordability of a Novel Gene Therapy in Hemophilia A ten Ham, Renske M.T.; Walker, Simon M.; Soares, Marta O.; More ten Ham, Renske M.T.; Walker, Simon M.; Soares, Marta O.; Frederix, Geert W.J.; Leebeek, Frank W.G.; Fischer, Kathelijn; Coppens, Michiel; Palmer, Stephen J. Less HemaSphere. 6(2):e679, February 2022. Abstract Abstract Favorites PDF Get Content & Permissions Go to Full Text of this Article Open SDC
Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm Baronciani, Donatella; Casale, Maddalena; De Franceschi, Lucia; More Baronciani, Donatella; Casale, Maddalena; De Franceschi, Lucia; Graziadei, Giovanna; Longo, Filomena; Origa, Raffaella; Rigano, Paolo; Pinto, Valeria; Marchetti, Monia; Gigante, Antonia; Iolascon, Achille; Forni, Gian Luca; (on behalf of, & Chair of, the EHA Scientific Working Group on Red Cells and Iron) Less HemaSphere. 5(5):e555, May 2021. Abstract Abstract Favorites PDF Get Content & Permissions Go to Full Text of this Article Open
Hemophilia Gene Therapy: Approaching the First Licensed Product Batty, Paul; Lillicrap, David Batty, Paul; Lillicrap, David Less HemaSphere. 5(3):e540, March 2021. Abstract Abstract Favorites PDF Get Content & Permissions Go to Full Text of this Article Open
Gene Therapy for Primary Immunodeficiency Houghton, Benjamin C.; Booth, Claire Houghton, Benjamin C.; Booth, Claire Less HemaSphere. 5(1):e509, January 2021. Abstract Abstract Favorites PDF Get Content & Permissions Go to Full Text of this Article Open
Gene Therapy of the Hemoglobinopathies Kunz, Joachim B.; Kulozik, Andreas E. Kunz, Joachim B.; Kulozik, Andreas E. Less HemaSphere. 4(5):e479, October 2020. Abstract Abstract Favorites PDF Get Content & Permissions Go to Full Text of this Article Open
