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Poster Session I: Sickle cell disease

PF736 ZINC FINGER NUCLEASE-MEDIATED DISRUPTION OF THE BCL11A ERYTHROID ENHANCER IN PLERIXAFOR MOBILIZED CD34+ CELLS RESULTS IN ENRICHED BIALLELEIC EDITING AND ALLELE-ADDITIVE INCREASES IN FETAL HEMOGLOBIN

Rimmele, P.1; Ling, H.1; Lessard, S.1; Moran, K.1; Vieira, B.1; Lin, Y.-D.1; Hong, V.1; Reik, A.2; Dang, D.2; Huttner, K.1; Hicks, A.1

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doi: 10.1097/01.HS9.0000561228.81599.cf
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Abstract

Copyright © 2019 the Author(s). Published by Wolters Kluwer Health, Inc. on behalf of the European Hematology Association.