Address correspondence to Dr Bo Hoon Lee, 601 Elmwood Ave, Box 631, Rochester, NY 14642, [email protected].
RELATIONSHIP DISCLOSURE: Dr Lee has received personal compensation in the range of $500 to $4,999 for serving on a scientific advisory or data safety monitoring board for AMO Pharma and F. Hoffmann-La Roche AG. The institution of Dr Lee has received research support from AMO Pharma, Novartis, Sanofi, and Sarepta Therapeutics.
UNLABELED USE OF PRODUCTS/INVESTIGATIONAL USE DISCLOSURE: Dr Lee discusses the unlabeled/investigational use of allogenic cell therapy, ataluren, follistatin, gene therapy, pamrevlumab, and vamorolone for the treatment of Duchenne muscular dystrophy.